Natural History Study for Patients With Nemaline Myopathy in the UK
NCT06670378 · Status: ACTIVE_NOT_RECRUITING · Type: OBSERVATIONAL · Enrollment: 45
Last updated 2026-04-13
Summary
The goal of this study is to to learn more about what assessments would be useful to measure for NM and what normally happens during the lives of people with NM to support future clinical trial development.
Conditions
- Nemaline Myopathy
Sponsors & Collaborators
-
Muscular Dystrophy UK
collaborator UNKNOWN -
University of Oxford
lead OTHER
Principal Investigators
-
Prof Laurent Servais · MDUK Oxford Neuromuscular Centre, University of Oxford
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2024-10-07
- Primary Completion
- 2029-08-31
- Completion
- 2029-08-31
Countries
- United Kingdom
Study Locations
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