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Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatments

NCT05768048 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 500

Last updated 2023-03-14

No results posted yet for this study

Summary

This is an observational multicenter retrospective and prospective study on natural history of SMA also considering the 'new natural history' secondary to the availability of commercially available therapies.

All the patients enrolled to date in the Italian registry, if not part of clinical trials, will be included in the present study.

Conditions

Sponsors & Collaborators

  • University of Milan

    collaborator OTHER

  • Bambino Gesù Hospital and Research Institute

    collaborator OTHER

  • University of Messina

    collaborator OTHER

  • Gaslini Children's Hospital

    collaborator OTHER

  • Fondazione Policlinico Universitario Agostino Gemelli IRCCS

    lead OTHER

Eligibility

Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2022-11-28
Primary Completion
2027-11-27
Completion
2027-11-27

Countries

  • Italy

Study Locations

More Related Trials

Entities

Diseases

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT05768048 on ClinicalTrials.gov