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Development of a Multidisciplinary Network for Clinical and Laboratory Research for SMA

NCT05866939 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 400

Last updated 2023-05-19

No results posted yet for this study

Summary

The goal of this observational study is to to establish profiles of clinical progression in patients affected by the different types of SMA (type I, II and III) treated with the currently approved drugs using a structured battery of clinical tests.

Another goal of the study is to assess the progression of the disease in patients identified through neonatal screening.

Conditions

Sponsors & Collaborators

  • Ospedale Pediatrico Bambin Gesù

    collaborator OTHER

  • IRCCS Eugenio Medea

    collaborator OTHER

  • Azienda Ospedaliera Universitaria Policlinico "G. Martino"

    collaborator OTHER

  • Fondazione Policlinico Universitario Agostino Gemelli IRCCS

    lead OTHER

Eligibility

Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2023-06-30
Primary Completion
2024-06-30
Completion
2025-06-30

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Entities

Diseases

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT05866939 on ClinicalTrials.gov