Observational Study of Neuromuscular Function in CMT Type 1&2 and Healthy Controls
NCT04980807 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 30
Last updated 2022-03-07
Summary
The primary aim of this study is to discover whether patients with CMT type 1 and 2 have neuromuscular junction transmission deficits.
The secondary aim is to collect information of different clinical and electrophysiological test procedures to perform possible future clinical trials in CMT patients.
Conditions
- Charcot-Marie-Tooth Disease
Sponsors & Collaborators
-
Aarhus University Hospital
collaborator OTHER -
Ohio State University
collaborator OTHER -
NMD Pharma A/S
lead INDUSTRY
Principal Investigators
-
Henning Andersen, MD, PhD · Aarhus University Hospital
-
William D Arnold, MD · Ohio State University
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- Yes
Timeline & Regulatory
- Start
- 2021-04-07
- Primary Completion
- 2022-03-03
- Completion
- 2022-03-03
Countries
- United States
- Denmark
Study Locations
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