A Registered Cohort Study on Duchenne Muscular Dystrophy
NCT04012671 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 2000
Last updated 2021-03-22
Summary
Dystrophinopathy is a term of X-linked recessive genetic disease, including Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and the X-linked dilated cardiomyopathy. The aim of this study is to determine the clinical spectrum and natural progression of dystrophinopathy in a prospective multicenter natural history study, to assess the clinical, genetic of patients with dystrophinopathy to optimize clinical management.
Conditions
Sponsors & Collaborators
-
Ning Wang, MD., PhD.
lead OTHER
Eligibility
- Min Age
- 2 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2019-07-01
- Primary Completion
- 2039-12-31
- Completion
- 2049-12-31
Countries
- China
Study Locations
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