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Nemaline Myopathy Clinical Research Network (NM-CTRN)

NCT06774703 · Status: NOT_YET_RECRUITING · Type: OBSERVATIONAL · Enrollment: 50

Last updated 2025-01-14

No results posted yet for this study

Summary

The goal of this study is to establish a research network to help define the natural disease history and clinical outcome measures for Nemaline Myopathy (NM).

Conditions

  • Nemaline Myopathy

Sponsors & Collaborators

Principal Investigators

  • Carolina Tesi-Rocha, MD · Stanford University

  • Tina Duong, PT, PhD · Stanford University

  • John W Day, MD, PhD · Stanford University

  • Leslie Hayes, MD · Boston Children's Hospital

  • Alan Beggs, PhD · Boston Children's Hospital

  • Jim Dowling, MD, PhD · The Hospital for Sick Children

  • Richard Finkel, MD · St Jude Children's Hospital

  • Carsten Bonnemann, MD, PhD · National Institutes of Health (NIH)

  • Kaitlin Batley, MD · UT Southwestern Medical Centre

Eligibility

Min Age
0 Years
Max Age
18 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2025-01-31
Primary Completion
2029-12-31
Completion
2029-12-31

Countries

  • United States
  • Canada

Study Locations

More Related Trials

Entities

Companies

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT06774703 on ClinicalTrials.gov