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Outcome Measures in Duchenne Muscular Dystrophy: A Natural History Study

NCT02780492 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 35

Last updated 2024-01-05

No results posted yet for this study

Summary

Novel emerging therapies for Duchenne Muscular Dystrophy (DMD) require a deeper understanding of DMD natural history. This study aim to assess the natural history of DMD through a composite assessment tool capable of capturing disease progression linking ambulant and non-ambulant phases of the disease.

Conditions

Interventions

OTHER

Set of assessment tools

Sponsors & Collaborators

  • Association Française contre les Myopathies (AFM), Paris

    collaborator OTHER

  • University of Newcastle Upon-Tyne

    collaborator OTHER

  • Groupe Hospitalier Pitie-Salpetriere

    collaborator OTHER

  • Leiden University Medical Center

    collaborator OTHER

  • Radboud University Medical Center

    collaborator OTHER

  • University College, London

    lead OTHER

Principal Investigators

  • Francesco Muntoni, PhD · Dubowitz Neuromuscular Centre, UCL-Institute of Child Health

Eligibility

Min Age
5 Years
Max Age
18 Years
Sex
MALE
Healthy Volunteers
Yes

Timeline & Regulatory

Start
2012-04-11
Primary Completion
2022-04-28
Completion
2022-04-28

Countries

  • France
  • Netherlands
  • United Kingdom

Study Locations

More Related Trials

Entities

Diseases

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT02780492 on ClinicalTrials.gov