phenotypeS in Non Ambulant Duchenne Muscular Dystrophy
NCT06366815 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 250
Last updated 2024-10-04
Summary
The aims of the study are to prospectively collect information on several aspects of function in non-ambulant DMD patients by using a structured battery of tests including motor, respiratory and cardiac function
Conditions
- Duchenne Muscular Dystrophy
- Natural History
- Motor Function; Retardation
Interventions
- OTHER
-
Different Phenotypes of non ambulant patients with Duchenne Muscular Dystrophy
clinical and functional data collection of non ambulant patients with Duchenne muscular dystrophy
Sponsors & Collaborators
-
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
lead OTHER
Principal Investigators
-
Marika Pane · Fondazione Policlinico Universitario A. Gemelli, IRCCS
Eligibility
- Min Age
- 8 Years
- Max Age
- 35 Years
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2022-08-30
- Primary Completion
- 2024-09-30
- Completion
- 2025-12-30
Countries
- Italy
Study Locations
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