Natural History Study of Patients With Limb-Girdle Muscular Dystrophy 2I
NCT03842878 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 52
Last updated 2026-02-12
Summary
Prospective, longitudinal, interventional, single-group, multicenter natural history study to better know the LGMD2I disease physiopathology. The duration of participation for each patient will be up to 24 months.
Conditions
- LGMD2I
Sponsors & Collaborators
-
Genethon
lead OTHER
Principal Investigators
-
John Vissing, PR · Professor of neurology
Eligibility
- Min Age
- 16 Years
- Max Age
- 99 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2020-02-19
- Primary Completion
- 2023-12-14
- Completion
- 2023-12-14
Countries
- Denmark
- France
- United Kingdom
Study Locations
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