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Clinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe)

NCT01611610 · Status: COMPLETED · Phase: NA · Type: INTERVENTIONAL · Enrollment: 4

Last updated 2014-03-05

No results posted yet for this study

Summary

The aim of this project is to establish a network of clinical teams including the major neuromuscular centers in Europe.

We plan to work together to find the best common outcome measures for the following multicenter therapeutic trials.

Conditions

Interventions

OTHER

Functional tests

The ambulant patients will perform * MFM (20 items) * Hammersmith modified module - MHMFS * Timed tests (time to rise from the floor,...) * 6 minute walk test * PedsQL - neuromuscular module

OTHER

Functional tests

The non-ambulant patients will perform: * MFM (20 items) * Hammersmith modified module - MHMFS * Upper Limb Functional Items * Egen Klassifikation 2 questionnaire - EK2 * PedsQL questionnaire - neuromuscular module

Sponsors & Collaborators

  • Institut de Myologie, France

    lead OTHER

Principal Investigators

  • Laurent Servais, MD, PhD · Institut de Myologie

Study Design

Allocation
NON_RANDOMIZED
Masking
NONE
Model
PARALLEL

Eligibility

Min Age
30 Months
Max Age
18 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2011-05-31
Primary Completion
2013-05-31
Completion
2013-05-31

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Entities

Diseases

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT01611610 on ClinicalTrials.gov