European Registry of Patients With Infantile-onset Spinal Muscular Atrophy
NCT03339830 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 100
Last updated 2021-09-13
Summary
IO-SMA-Registry is a prospective, longitudinal and observational study which objective is to collect prospectively information on longevity, psychomotor development and respiratory function of patients with infantile-onset spinal muscular atrophy.
Conditions
Sponsors & Collaborators
-
Institut de Myologie, France
lead OTHER
Principal Investigators
-
Laurent Servais, MD, PhD · Institute of Myology
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2017-10-10
- Primary Completion
- 2020-11-15
- Completion
- 2020-11-15
Countries
- France
Study Locations
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