Therapeutic Management and Use of Resources and Costs of Spinal Muscular Atrophy in Spain
NCT06632730 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 69
Last updated 2024-10-09
Summary
An observational, retrospective, cross-sectional, multicenter study. Real-world data were obtained from medical records of Spanish public hospitals (9 hospitals).
Conditions
- Spinal Muscular Atrophy Type I
- Spinal Muscular Atrophy Type II
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Novartis Pharmaceuticals · Novartis Pharmaceuticals
Eligibility
- Max Age
- 14 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2023-07-05
- Primary Completion
- 2023-11-20
- Completion
- 2023-11-20
Countries
- United States
Study Locations
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