Adult Spinal Muscular Atrophy (SMA) China Registry
NCT05618379 · Status: ACTIVE_NOT_RECRUITING · Type: OBSERVATIONAL · Enrollment: 200
Last updated 2025-07-11
Summary
The primary objective of the study is to describe the natural history and utilization of disease modifying therapy (DMT) among adult Chinese participants with SMA linked to chromosome 5q (5q-SMA).
Conditions
- Muscular Atrophy, Spinal
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Medical Director · Biogen
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2023-01-06
- Primary Completion
- 2028-06-01
- Completion
- 2028-06-01
Countries
- China
Study Locations
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