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Clinical Study of Spinal Muscular Atrophy

NCT00443066 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 120

Last updated 2023-03-21

No results posted yet for this study

Summary

The investigators propose to prepare for clinical trials where SMA patients are asked to join the research effort. The visits will include questions, physical exam, blood drawing, and sometimes X-rays and a skin biopsy. The investigators will use modern computer methods to process the information during which the investigators will plan a clinical trial. Once the clinical trial begins, the investigators will offer SMA patients participation if they meet the criteria for that trial.

Identifying an effective SMA treatment is very important because there is currently none. Clinical trials are the only way to decide whether a new treatment works in SMA patients or not.

Conditions

Sponsors & Collaborators

Principal Investigators

  • Darryl C De Vivo, MD · Columbia University

Eligibility

Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2005-05-31
Primary Completion
2011-08-17
Completion
2011-08-17

Countries

  • United States

Study Locations

More Related Trials

Entities

Diseases
Companies

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT00443066 on ClinicalTrials.gov