Natural History of Types 2 and 3 SMA in Taiwan
NCT03300869 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 300
Last updated 2019-07-26
Summary
The primary objective of this study is to investigate the natural history of spinal muscular atrophy (SMA) types 2 and 3 patients in Taiwan. This study will provide further insights into the clinical course SMA. Several analyses will be conducted regarding overall survival, demographic characteristics, motor function, respiratory and nutritional support, and genotype and phenotype correlation.
Conditions
Sponsors & Collaborators
- collaborator INDUSTRY
-
National Taiwan University Hospital
collaborator OTHER -
Mackay Memorial Hospital
collaborator OTHER -
China Medical University Hospital
collaborator OTHER -
Changhua Christian Hospital
collaborator OTHER -
Chang Gung Memorial Hospital
collaborator OTHER -
Kaohsiung Medical University Chung-Ho Memorial Hospital
lead OTHER
Eligibility
- Min Age
- 6 Months
- Max Age
- 70 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2017-09-01
- Primary Completion
- 2019-12-31
- Completion
- 2019-12-31
Countries
- Taiwan
Study Locations
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