Natural History of Types 2 and 3 SMA in Taiwan

NCT03300869 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 300

Last updated 2019-07-26

No results posted yet for this study

Summary

The primary objective of this study is to investigate the natural history of spinal muscular atrophy (SMA) types 2 and 3 patients in Taiwan. This study will provide further insights into the clinical course SMA. Several analyses will be conducted regarding overall survival, demographic characteristics, motor function, respiratory and nutritional support, and genotype and phenotype correlation.

Conditions

Sponsors & Collaborators

  • Biogen

    collaborator INDUSTRY
  • National Taiwan University Hospital

    collaborator OTHER
  • Mackay Memorial Hospital

    collaborator OTHER
  • China Medical University Hospital

    collaborator OTHER
  • Changhua Christian Hospital

    collaborator OTHER
  • Chang Gung Memorial Hospital

    collaborator OTHER
  • Kaohsiung Medical University Chung-Ho Memorial Hospital

    lead OTHER

Eligibility

Min Age
6 Months
Max Age
70 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2017-09-01
Primary Completion
2019-12-31
Completion
2019-12-31

Countries

  • Taiwan

Study Locations

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Entities

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT03300869 on ClinicalTrials.gov