Improving Standards of Care and Translational Research in Spinal Muscular Atrophy (SMA)
NCT03520179 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 600
Last updated 2022-08-17
Summary
The SMA REACH UK Network is a national and international partnership between doctors and therapists involved in the care of children and adults with Spinal Muscular Atrophy. This network is supported by Biogen and SMA UK.
Conditions
Sponsors & Collaborators
-
Great Ormond Street Hospital for Children NHS Foundation Trust
lead OTHER
Eligibility
- Min Age
- 0 Months
- Max Age
- 99 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2013-12-17
- Primary Completion
- 2023-08-12
- Completion
- 2023-08-12
Countries
- United Kingdom
Study Locations
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