A Study to Collect Blood Samples From Patients With Spinal Muscular Atrophy for Biomarker Analysis

Adults With SMA Treated With Nusinersen

NCT04591678 ·Status: COMPLETED

Home Monitoring of Adult Patients With SMA: a Pilot Multicenter Validation Study

NCT05839145 ·Status: NOT_YET_RECRUITING ·Phase: NA

Muscular Biomarkers in Amyotrophic Lateral Sclerosis

NCT02670226 ·Status: COMPLETED ·Phase: NA

Validation of Biomarkers in Amyotrophic Lateral Sclerosis (ALS)

NCT00677768 ·Status: COMPLETED

Clinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe)

NCT01611610 ·Status: COMPLETED ·Phase: NA

New Imaging Biomarkers for Muscular Diseases - Multispectral Optoacoustic Imaging in Spinal Muscular Atrophy

NCT04115475 ·Status: COMPLETED ·Phase: NA

Clinical Study of Spinal Muscular Atrophy

NCT00443066 ·Status: COMPLETED

Adult Spinal Muscular Atrophy (SMA) China Registry

NCT05618379 ·Status: ACTIVE_NOT_RECRUITING

Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients with Spinal Muscular Atrophy Type 1

NCT05614531 ·Status: ENROLLING_BY_INVITATION ·Phase: PHASE1/PHASE2

Pediatric Spinal Muscular Atrophy (SMA) China Registry

NCT05042921 ·Status: ACTIVE_NOT_RECRUITING

Long-term Follow-up of Patients With Spinal Muscular Atrophy Treated With OAV101 in Clinical Trials

NCT05335876 ·Status: RECRUITING ·Phase: PHASE3

Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies

NCT06532474 ·Status: RECRUITING

Prospective Study of the Natural History of Patients With Type 2 and 3 Spinal Muscular Atrophy

NCT02391831 ·Status: COMPLETED ·Phase: NA

Imaging and BioFluid Biomarkers in Amyotrophic Lateral Sclerosis

NCT02559869 ·Status: COMPLETED

Spinal Muscular Atrophy (SMA) Biomarkers Study in the Immediate Postnatal Period of Development

NCT01736553 ·Status: COMPLETED

Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophy

NCT06888661 ·Status: ENROLLING_BY_INVITATION ·Phase: EARLY_PHASE1

Clinical Trial of Exercise in Patients With Spinal Muscular Atrophy (SMA)

NCT01166022 ·Status: COMPLETED ·Phase: NA

Study of SPG302 in Healthy Volunteers and ALS Participants

NCT05882695 ·Status: COMPLETED ·Phase: PHASE1

A Study to Learn About the Long-Term Safety of Higher Doses of Nusinersen (BIIB058) Given as Injections to Participants With Spinal Muscular Atrophy (SMA) Who Took Part in an Earlier Nusinersen Trial (ONWARD)

NCT04729907 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE3

Randomized Double-Blind Placebo-Controlled Adaptive Design Trial Of Intrathecally Administered Autologous Mesenchymal Stem Cells In Multiple System Atrophy

NCT05167721 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE2

Natural History of Types 2 and 3 SMA in Taiwan

NCT03300869 ·Status: UNKNOWN

Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients

NCT05901987 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1/PHASE2

Newborn Screening for Spinal Muscular Atrophy

NCT02123186 ·Status: COMPLETED

Study of Nusinersen (BIIB058) in Participants With Spinal Muscular Atrophy

NCT04089566 ·Status: COMPLETED ·Phase: PHASE3

Target ALS Biomarker Study; Longitudinal Biofluids, Clinical Measures, and At Home Measures

NCT05137665 ·Status: RECRUITING