Natural History of Duchenne Muscular Dystrophy
NCT03882827 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 220
Last updated 2026-02-12
Summary
Baseline Study on Duchenne Muscular Dystrophy (DMD) in view to collect data on the natural disease course in a cohort in young male subjects aged from 4 to 9 Years over a period of 6 to 36 months using disease appropriate evaluations.
Conditions
Sponsors & Collaborators
-
Genethon
lead OTHER
Principal Investigators
-
Francesco MUNTONI, Pr · GOSH LONDON
Eligibility
- Min Age
- 4 Years
- Max Age
- 9 Years
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2019-12-19
- Primary Completion
- 2029-05-30
- Completion
- 2029-09-30
Countries
- Belgium
- France
- Spain
- United Kingdom
Study Locations
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