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Observational Study of Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 Skipping

NCT01385917 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 45

Last updated 2016-04-12

No results posted yet for this study

Summary

PreU7-53 is a natural history study. The objective is to monitor the clinical and radiological course of upper limb muscle impairment in patients with Duchenne Muscular Dystrophy (DMD), potentially treatable with AAV-mediated exon 53 skipping.

Conditions

Sponsors & Collaborators

  • Institute of Myology

    collaborator OTHER

  • Genethon

    lead OTHER

Principal Investigators

  • Laurent SERVAIS, MD · Myology Institute

Eligibility

Min Age
12 Years
Max Age
20 Years
Sex
MALE
Healthy Volunteers
No

Timeline & Regulatory

Start
2011-10-31
Primary Completion
2018-12-31
Completion
2018-12-31

Countries

  • France
  • United Kingdom

Study Locations

More Related Trials

Entities

Diseases

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT01385917 on ClinicalTrials.gov