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Limb-Girdle Video Assessment

NCT05528757 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 45

Last updated 2023-12-18

No results posted yet for this study

Summary

The purpose of this study is to develop a new remote-based video assessment outcome measure for Limb-Girdle Muscular Dystrophy (LGMD) trials. The overall objectives for this study are: 1. Identify domains and tasks meaningful to participants with a Limb-Girdle Muscular Dystrophy (LGMD) for development of the LGVA, including considerations for subtype heterogeneity and functional subgroup branching; 2. Determine the feasibility and reliability of the LGVA with test-retest of the LGVA Video Capture Manual; 3. Assess and refine the LGVA Video Capture Manual to ensure standardization and incorporate feedback from participants; 4. Collect source material videos using the LGVA Video Capture Manual to support the development of scorecards for the LGVA.

Conditions

  • Limb-Girdle Muscular Dystrophy ; Subtypes 2A, 2B, and 2I

Sponsors & Collaborators

  • Coalition to Cure Calpain 3 (C3)

    collaborator UNKNOWN

  • Jain Foundation

    collaborator OTHER

  • The Emmes Company, LLC

    lead INDUSTRY

Principal Investigators

  • Lauren Carroll · Casimir

Eligibility

Min Age
14 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2022-06-20
Primary Completion
2022-11-02
Completion
2022-11-02

Countries

  • United States

Study Locations

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Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT05528757 on ClinicalTrials.gov