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Limb Girdle Muscular Dystrophy (LGMD) Natural History

NCT01783509 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 13

Last updated 2022-04-28

No results posted yet for this study

Summary

The purpose of this study is to understand more about limb-girdle muscular dystrophy. Therefore, the investigators would like to track the following information collected once a year from patients with GENETICALLY CONFIRMED LGMD: quality of life questionnaires, muscle strength, motor function, routine examination, assessment of patient (or parent) understanding of LGMD, and serum (blood) for growth factors, cytokines, and biomarkers (all parts of your blood). By tracking this information, we hope to be able to understand more about the diagnosis, progression and natural history of this disorder.

Conditions

  • Muscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)

Sponsors & Collaborators

Principal Investigators

  • Ibrahim Binalsheikh, MD · Carolinas Medical Center - Pediatrics

Eligibility

Min Age
6 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2011-11-30
Primary Completion
2017-07-31
Completion
2017-07-31

Countries

  • United States

Study Locations

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Entities

Companies

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT01783509 on ClinicalTrials.gov