Long-Term Development of Muscular Dystrophy Outcome Assessments
NCT05989620 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 1000
Last updated 2025-11-18
Summary
This is a 24-month, observational study of up to 1000 participants with Limb Girdle Muscular Dystrophy (LGMD), Myotonic Dystrophy Type 2 (DM2), and late onset Pompe disease (LOPD).
Conditions
- LGMD1B
- LGMD1C
- LGMD1D
- LGMD1E
- LGMD1F
- LGMD1G
- LGMD1H
- LGMD2A
- LGMD2B
- LGMD2C
- LGMD2D
- LGMD2E
- LGMD2F
- LGMD2G
- LGMD2I
- LGMD2J
- LGMD2K
- LGMD2L
- LGMD2M
- LGMD2N
- LGMD2O
- LGMD2P
- LGMD2Q
- LGMD2S
- LGMD2T
- LGMD2U
- LGMD2W
- LGMD2X
- LGMD2Y
Sponsors & Collaborators
-
Muscular Dystrophy Association
collaborator OTHER -
Virginia Commonwealth University
lead OTHER
Principal Investigators
-
Nicholas Johnson, MD · Virginia Commonwealth University
Eligibility
- Min Age
- 6 Years
- Max Age
- 50 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2023-10-18
- Primary Completion
- 2028-10-01
- Completion
- 2029-05-01
Countries
- United States
Study Locations
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