Limb Girdle Muscular Dystrophy Type 2E Recruitment Study

NCT03492346 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 25

Last updated 2023-03-06

No results posted yet for this study

Summary

This study is to recruit and establish baseline measurements for potential subjects that may be eligible for a gene therapy trial. Specifically, this trial is recruiting individuals who are suspected or have been confirmed to have Limb Girdle Muscular Dystrophy type 2E (LGMD2E).

Conditions

  • Limb-Girdle Muscular Dystrophy, Type 2E

Sponsors & Collaborators

  • Myonexus Therapeutics

    collaborator UNKNOWN
  • Nationwide Children's Hospital

    lead OTHER

Principal Investigators

  • Jerry R Mendell, M.D. · Nationwide Children's Hospital

Eligibility

Min Age
3 Years
Max Age
15 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2018-03-28
Primary Completion
2023-03-28
Completion
2023-03-28

Countries

  • United States

Study Locations

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Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT03492346 on ClinicalTrials.gov