Limb Girdle Muscular Dystrophy Type 2E Recruitment Study
NCT03492346 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 25
Last updated 2023-03-06
Summary
This study is to recruit and establish baseline measurements for potential subjects that may be eligible for a gene therapy trial. Specifically, this trial is recruiting individuals who are suspected or have been confirmed to have Limb Girdle Muscular Dystrophy type 2E (LGMD2E).
Conditions
- Limb-Girdle Muscular Dystrophy, Type 2E
Sponsors & Collaborators
-
Myonexus Therapeutics
collaborator UNKNOWN -
Nationwide Children's Hospital
lead OTHER
Principal Investigators
-
Jerry R Mendell, M.D. · Nationwide Children's Hospital
Eligibility
- Min Age
- 3 Years
- Max Age
- 15 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2018-03-28
- Primary Completion
- 2023-03-28
- Completion
- 2023-03-28
Countries
- United States
Study Locations
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