Clinical Trial Readiness for the Dystroglycanopathies
NCT00313677 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 190
Last updated 2025-07-30
Summary
The purpose of the study is to describe the early signs and symptoms of the dystroglycanopathies, and to gather information that will be required for future clinical trials.
Conditions
- Muscular Dystrophy
Sponsors & Collaborators
-
National Institute of Neurological Disorders and Stroke (NINDS)
collaborator NIH -
Katherine Mathews
lead OTHER
Principal Investigators
-
Katherine Mathews, M.D. · University of Iowa
-
Kevin Campbell, Ph.D. · Co-Investigator
-
Steven A. Moore, M.D. Ph.D. · Co-Investigator
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2006-04-30
- Primary Completion
- 2030-07-31
- Completion
- 2030-07-31
Countries
- United States
Study Locations
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