Natural History Study of MNGIE
NCT04245917 · Status: SUSPENDED · Type: OBSERVATIONAL · Enrollment: 60
Last updated 2021-07-22
Summary
Non-interventional, prospective, multicenter, natural history study of patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE)
Conditions
- Mitochondrial Neurogastrointestinal Encephalomyopathy
Interventions
- OTHER
-
Non-interventional
Non-interventional natural history study
Sponsors & Collaborators
-
Entrada Therapeutics, Inc.
lead INDUSTRY
Principal Investigators
-
Michio Hirano, MD · Columbia University
Eligibility
- Min Age
- 5 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2020-08-06
- Primary Completion
- 2025-02-28
- Completion
- 2026-02-28
Countries
- United States
- Turkey (Türkiye)
Study Locations
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