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Natural History Study of Patients With Centronuclear Myopathies

NCT04977648 · Status: WITHDRAWN · Type: OBSERVATIONAL

Last updated 2022-07-11

No results posted yet for this study

Summary

This is a prospective, longitudinal study of the natural disease course intended to recruit approximately 60 patients with centronuclear myopathies (CNM) in Europe and the United States. The duration of the study, including the enrollment period, will be approximately 4 years. Data from the study will be used to characterize the natural disease course of CNM, to identify prognostic variables of the disease and to determine the best outcome measure(s) for the evaluation of future therapeutic approaches.

Conditions

  • Centronuclear Myopathy

Sponsors & Collaborators

  • Dynacure

    lead INDUSTRY

Eligibility

Min Age
0 Months
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2022-09-30
Primary Completion
2026-03-31
Completion
2026-03-31

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Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT04977648 on ClinicalTrials.gov