New Imaging Biomarkers for Muscular Diseases - Multispectral Optoacoustic Imaging in Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- NA
Clinical Trials Related to Spinal Muscular Atrophy
Related studies linked through entity extraction aliases.
Pulmonary Function Test Changes and Respiratory Muscle Strength Trends in Spinal Muscular Atrophy Patients Receiving Nusinersen Treatments
- Status
- WITHDRAWN
- Phase
- EARLY_PHASE1
A Registered Cohort Study on SMA
- Status
- RECRUITING
- Phase
- N/A
A Drug-drug Interaction Study With Risdiplam Multiple Dose and Midazolam in Healthy Participants
- Status
- COMPLETED
- Phase
- PHASE1
Fat and Glucose Metabolism in Fed and Fasted State in Patients With Low Skeletal Muscle Mass
- Status
- COMPLETED
- Phase
- NA
AveXis Managed Access Program Cohort for Access to AVXS-101
- Status
- APPROVED_FOR_MARKETING
- Phase
- N/A
An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- PHASE2
Reliability and Validity of the ACTIVE-mini for Quantifying Movement in Infants With Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- N/A
Spinraza in Adult Spinal Muscular Atrophy
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- N/A
Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and Biofeedback
- Status
- COMPLETED
- Phase
- NA
Early Check: Expanded Screening in Newborns
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
Sun May Arise on SMA : Newborn Screening of Spinal Muscular Atrophy in Belgium
- Status
- COMPLETED
- Phase
- N/A
Improving Standards of Care and Translational Research in Spinal Muscular Atrophy (SMA)
- Status
- UNKNOWN
- Phase
- N/A
Pre-Symptomatic Study of Intravenous Onasemnogene Abeparvovec-xioi in Spinal Muscular Atrophy (SMA) for Patients With Multiple Copies of SMN2
- Status
- COMPLETED
- Phase
- PHASE3
Study of Intrathecal Administration of Onasemnogene Abeparvovec-xioi for Spinal Muscular Atrophy
- Status
- TERMINATED
- Phase
- PHASE1
European Registry of Patients With Infantile-onset Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- N/A
Natural History of Types 2 and 3 SMA in Taiwan
- Status
- UNKNOWN
- Phase
- N/A
Development of a Space Exploration Assessment for Children With Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- NA
Neonatal Spinal Muscular Atrophy (SMA) Screening
- Status
- RECRUITING
- Phase
- N/A
A Study of Risdiplam (RO7034067) in Adult and Pediatric Participants With Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- PHASE2