A Study of the Safety and Effectiveness of Onasemnogene Abeparvovec (Zolgensma) Intrathecal Injection in Spinal Muscular Atrophy Patients
- Status
- NOT_YET_RECRUITING
- Phase
- N/A
Clinical Trials Related to Spinal Muscular Atrophy
Related studies linked through entity extraction aliases.
A Real-World Medical Chart Review of Spinal Muscular Atrophy Patients Treated With Onasemnogene Abeparvovec in Saudi Arabia
- Status
- NOT_YET_RECRUITING
- Phase
- N/A
Spinal Muscular Atrophy and School Transitions
- Status
- NOT_YET_RECRUITING
- Phase
- N/A
Effects of Developmental Support for Mothers of Infants With Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- NA
Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
- Status
- RECRUITING
- Phase
- NA
ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
- Status
- NOT_YET_RECRUITING
- Phase
- PHASE4
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Status
- RECRUITING
- Phase
- PHASE3
CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain
- Status
- RECRUITING
- Phase
- N/A
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- Status
- RECRUITING
- Phase
- PHASE2
Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
- Status
- RECRUITING
- Phase
- N/A
Respiratory Functions, Thoracoabdominal Movements and Exercise Capacity in Neuromuscular Diseases
- Status
- RECRUITING
- Phase
- N/A
Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular Disorders
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
A Long-term Follow-up Study Evaluating Intravenous Injection of EXG001-307 in Patients With Type 1 SMA
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
- Status
- RECRUITING
- Phase
- N/A
Acceptability, Feasibility, Safety and Efficacy of a Optimized Rehabilitation Program for Treated Patients With Spinal Muscular Atrophy (SMA).
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- NA
A Registry Based Randomized-Controlled Trial of an Upper Limb Exergaming Intervention for Children and Adolescents With Spinal Muscular Atrophy
- Status
- RECRUITING
- Phase
- NA
High-intensity Interval Training in Patients With Spinal Muscular Atrophy
- Status
- RECRUITING
- Phase
- NA
Characterization of New Phenotypes of Patients With Spinal Muscular Atrophy Treated With SMN Restoring Therapy
- Status
- RECRUITING
- Phase
- NA
Spinal Muscular Atrophy Neonatal Screening Program
- Status
- RECRUITING
- Phase
- N/A
Spinal Cord Stimulation for the Treatment of Motor Deficits in People With Spinal Muscular Atrophy - Upper Limb
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- NA