SPACE Trial: Pyridostigmine vs Placebo in SMA Types 2, 3 and 4
- Status
- COMPLETED
- Phase
- PHASE2
Clinical Trials Related to Spinal Muscular Atrophy
Related studies linked through entity extraction aliases.
Prospective Evaluation of Infants With Spinal Muscular Atrophy:
- Status
- UNKNOWN
- Phase
- N/A
A Study of CK-2127107 in Patients With Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- PHASE2
A Study to Investigate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Risdiplam (RO7034067) Given by Mouth in Healthy Volunteers
- Status
- COMPLETED
- Phase
- PHASE1
A Study for Participants With Spinal Muscular Atrophy (SMA) Who Previously Participated in Nusinersen (ISIS 396443) Investigational Studies
- Status
- COMPLETED
- Phase
- PHASE3
Identification of a Biomarker Associated With Cis-duplication of the SMN1 Gene
- Status
- TERMINATED
- Phase
- NA
Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases
- Status
- COMPLETED
- Phase
- N/A
A Study to Assess the Safety and Tolerability of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy (SMA).
- Status
- TERMINATED
- Phase
- PHASE2
Effects of Standing on Non-Ambulatory Children With Neuromuscular Conditions
- Status
- COMPLETED
- Phase
- NA
A Study of Multiple Doses of Nusinersen (ISIS 396443) Delivered to Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- PHASE2
A Study to Assess the Efficacy and Safety of Nusinersen (ISIS 396443) in Participants With Later-onset Spinal Muscular Atrophy (SMA)
- Status
- COMPLETED
- Phase
- PHASE3
An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA)
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
Study of Feasibility to Reliably Measure Functional Abilities' Changes in Nonambulant Neuromuscular Patients Without Trial Site Visiting
- Status
- WITHDRAWN
- Phase
- NA
Reciprocating Gait Orthoses for Paraplegia Patients
- Status
- UNKNOWN
- Phase
- NA
WREX Outcome Study
- Status
- COMPLETED
- Phase
- N/A
A Study to Assess the Efficacy and Safety of Nusinersen (ISIS 396443) in Infants With Spinal Muscular Atrophy
- Status
- TERMINATED
- Phase
- PHASE3
National Registry for Egyptian Pediatric Neuromuscular Diseases
- Status
- UNKNOWN
- Phase
- N/A
Newborn Screening for Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- N/A
An Open-label Safety and Tolerability Study of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy (SMA) Who Previously Participated in ISIS 396443-CS2 (NCT01703988) or ISIS 396443-CS10 (NCT01780246)
- Status
- COMPLETED
- Phase
- PHASE1
Aerobic Training in Patients With Spinal Muscular Atrophy Type III
- Status
- COMPLETED
- Phase
- NA