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Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

NCT06955897 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 45

Last updated 2026-05-14

No results posted yet for this study

Summary

The purpose of this project is to investigate the utility of the SMA EFFORT, an SMA-specific patient-reported outcome measure, to assess perceived physical fatigability that is anchored to intensity and duration of activities. We aim to characterize perceived physical fatigability (PPF) in a diverse cohort of people with SMA (pwSMA) and evaluate the change of PPF before and after nusinersen dosing.

Conditions

Interventions

OTHER

Observational

Observational

Sponsors & Collaborators

Principal Investigators

  • Jacqueline Montes, Pt, EdD · Columbia University

Eligibility

Min Age
12 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2025-04-24
Primary Completion
2026-12-07
Completion
2027-02-26

Countries

  • United States

Study Locations

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Entities

Diseases
Companies

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT06955897 on ClinicalTrials.gov