Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE3
Clinical Trials Related to Duchenne Muscular Dystrophy
Related studies linked through entity extraction aliases.
AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications.
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
Wearable Technology to Assess Gait Function in SMA and DMD
- Status
- COMPLETED
- Phase
- N/A
A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of AMONDYS 45, EXONDYS 51, VYONDYS 53 in Subjects With DuchenneMuscular Dystrophy Carrying Eligible DMD Duplications.
- Status
- COMPLETED
- Phase
- PHASE2
Aerobic Exercise in Duchenne Muscular Dystrophy
- Status
- COMPLETED
- Phase
- NA
Exploratory Study of NS-089/NCNP-02 in DMD
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease
- Status
- COMPLETED
- Phase
- N/A
Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53)
- Status
- COMPLETED
- Phase
- PHASE3
A Registered Cohort Study on Duchenne Muscular Dystrophy
- Status
- RECRUITING
- Phase
- N/A
Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Expansion (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatment
- Status
- TERMINATED
- Phase
- PHASE2
A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) Who Have Completed Study 4658-102 (NCT03218995)
- Status
- TERMINATED
- Phase
- PHASE2
The Burden of Access in Duchenne Muscular Dystrophy in the US
- Status
- COMPLETED
- Phase
- N/A
Physical Activity Level of Norwegian Boys with Duchenne Muscular Dystrophy
- Status
- COMPLETED
- Phase
- N/A
Single Escalating Dose Pilot Trial of Canakinumab (ILARIS®) in Duchenne Muscular Dystrophy
- Status
- UNKNOWN
- Phase
- PHASE1/PHASE2
An Open-Label Extension Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy
- Status
- TERMINATED
- Phase
- PHASE3
Efficacy and Safety Study of WVE-210201 (Suvodirsen) With Open-label Extension in Ambulatory Patients With Duchenne Muscular Dystrophy
- Status
- TERMINATED
- Phase
- PHASE2/PHASE3
Natural History of Duchenne Muscular Dystrophy
- Status
- RECRUITING
- Phase
- N/A
Expanded Access Protocol for Boys With Duchenne Muscular Dystrophy
- Status
- AVAILABLE
- Phase
- N/A
Parent and Infant Inter(X)Action Intervention (PIXI)
- Status
- ENROLLING_BY_INVITATION
- Phase
- NA
A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With Ataluren
- Status
- COMPLETED
- Phase
- PHASE2