Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing Setting
- Status
- NOT_YET_RECRUITING
- Phase
- PHASE4
Clinical Trials Related to Duchenne Muscular Dystrophy
Related studies linked through entity extraction aliases.
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
- Status
- RECRUITING
- Phase
- PHASE2
Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy
- Status
- ENROLLING_BY_INVITATION
- Phase
- PHASE2
Investigation of the Effects of Functional Inspiratory Muscle Training Applied With Tele-Rehabilitation on Respiratory and Functional Parameters and Quality of Life in Children With Duchenne Muscular Dystrophy: Randomized Controlled Study
- Status
- COMPLETED
- Phase
- NA
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
- Status
- RECRUITING
- Phase
- PHASE3
Investigation of the Relationship Between Executive Functions and Occupational Performance of Children With Duchenne Muscular Dystrophy
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
Estimation of Non-Reimbursable Costs for Patients With Duchenne Muscular Dystrophy in France
- Status
- RECRUITING
- Phase
- N/A
A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)
- Status
- RECRUITING
- Phase
- PHASE1
Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old
- Status
- RECRUITING
- Phase
- PHASE2
Respiratory Functions, Thoracoabdominal Movements and Exercise Capacity in Neuromuscular Diseases
- Status
- RECRUITING
- Phase
- N/A
Evaluation of Brain Dysfunction in Patients with Duchene Muscular Dystrophy
- Status
- NOT_YET_RECRUITING
- Phase
- N/A
A Study on Safety and Effectiveness of Long-term Treatment With Vamorolone in Boys With Duchenne Muscular Dystrophy
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE4
The U.K. NorthStar Clinical Network
- Status
- NOT_YET_RECRUITING
- Phase
- N/A
Trial of Cell Based Therapy for DMD
- Status
- RECRUITING
- Phase
- PHASE1
A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
A Gene Transfer Therapy to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Therapeutic Plasma Exchange (Plasmapheresis) in Participants With Duchenne Muscular Dystrophy (DMD) and Pre-existing Antibodies to AAVrh74
- Status
- TERMINATED
- Phase
- PHASE1
Development of a Registry to Assess Natural History in Duchenne Muscular Dystrophy
- Status
- NOT_YET_RECRUITING
- Phase
- N/A
Expanded Access Study of UC-MSC in DMD Patients
- Status
- AVAILABLE
- Phase
- N/A
First in Human SAD/MAD Safety and PK Study With Adult DMD Safety and PK Cohort
- Status
- COMPLETED
- Phase
- EARLY_PHASE1
Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
- Status
- RECRUITING
- Phase
- N/A