NCT04120168 Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease Status COMPLETED Phase N/A
NCT04060199 Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53) Status COMPLETED Phase PHASE3
NCT04004065 Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Expansion (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatment Status TERMINATED Phase PHASE2
NCT03985878 A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) Who Have Completed Study 4658-102 (NCT03218995) Status TERMINATED Phase PHASE2
NCT03947112 Physical Activity Level of Norwegian Boys with Duchenne Muscular Dystrophy Status COMPLETED Phase N/A
NCT03936894 Single Escalating Dose Pilot Trial of Canakinumab (ILARIS®) in Duchenne Muscular Dystrophy Status UNKNOWN Phase PHASE1/PHASE2
NCT03917719 An Open-Label Extension Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy Status TERMINATED Phase PHASE3
NCT03907072 Efficacy and Safety Study of WVE-210201 (Suvodirsen) With Open-label Extension in Ambulatory Patients With Duchenne Muscular Dystrophy Status TERMINATED Phase PHASE2/PHASE3
NCT03863119 Expanded Access Protocol for Boys With Duchenne Muscular Dystrophy Status AVAILABLE Phase N/A
NCT03836300 Parent and Infant Inter(X)Action Intervention (PIXI) Status ENROLLING_BY_INVITATION Phase NA
NCT03796637 A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With Ataluren Status COMPLETED Phase PHASE2
NCT03786913 Quantitative Muscle Ultrasound as a Marker of Progression in Children With Muscular Diseases Status COMPLETED Phase N/A
NCT03760029 A Natural History Study In Chinese Male Patients With Duchenne Muscular Dystrophy Status COMPLETED Phase NA
NCT03689660 Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and Biofeedback Status COMPLETED Phase NA