The World Federation of Hemophilia Gene Therapy Registry
NCT04883710 · Status: NOT_YET_RECRUITING · Type: OBSERVATIONAL · Enrollment: 5000
Last updated 2021-05-12
Summary
The aim of the WFH GTR is to provide a database in which long-term data on PWH who receive gene therapy from around the world, will be collected and housed.
Conditions
Interventions
- OTHER
-
Gene therapy
This is a prospective patient registry.
Sponsors & Collaborators
-
World Federation of Hemophilia
lead OTHER
Eligibility
- Min Age
- 0 Years
- Max Age
- 100 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2022-01-01
- Primary Completion
- 2050-01-01
- Completion
- 2050-01-01
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