An Exploration of the Impact of Gene Therapy on the Lives of People With Haemophilia and Their Families
NCT04723680 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 69
Last updated 2023-03-01
Summary
This study programme aims to examine the real-world experience and impact of gene therapy in a diverse community of people and families affected by haemophilia who have been or will be exposed to gene therapy.
Conditions
Interventions
- OTHER
-
Qualitative interview
Qualitative semi structured interview
Sponsors & Collaborators
-
UniQure Biopharma B.V.
collaborator INDUSTRY -
Haemnet
lead OTHER
Principal Investigators
-
Simon P Fletcher · Researcher
Eligibility
- Min Age
- 16 Years
- Max Age
- 100 Years
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2020-08-13
- Primary Completion
- 2023-02-28
- Completion
- 2023-02-28
Countries
- United Kingdom
Study Locations
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