Screening for Lysosomal Acid Lipase Deficiency
NCT02926872 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 22
Last updated 2017-06-16
Summary
The primary outcome of this study is the development of a clinical profile of pediatric patients with LAL-D, which will enable the Sponsor to provide more focused guidance to the medical community as to which pediatric patients should be tested for LAL-D.
Conditions
- Lysosomal Acid Lipase Deficiency
Interventions
- OTHER
-
There is no intervention in the study
Sponsors & Collaborators
-
Alexion Pharmaceuticals, Inc.
lead INDUSTRY
Eligibility
- Min Age
- 2 Years
- Max Age
- 16 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2016-11-30
- Primary Completion
- 2017-06-05
- Completion
- 2017-06-05
Countries
- United States
Study Locations
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