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Lifetime Impact Study for Achondroplasia

NCT03872531 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 173

Last updated 2021-04-05

No results posted yet for this study

Summary

Observational study looking at the burden of illness in achondroplasia subjects aged 3 and above. The study will include a 3 year review of historical clinical data as well as a single point collection of questionnaire data to look at the impact on the following in individuals with achondroplasia versus a normative population:

* Quality of life
* Clinical burden
* Healthcare resource use
* Socio-economic burden
* Psychosocial burden

Up to 175 subjects will be enrolled in sites in Argentina, Colombia and Brazil.

Conditions

Sponsors & Collaborators

Principal Investigators

  • Medical Director · BioMarin Pharmaceutical

Eligibility

Min Age
3 Years
Max Age
100 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2019-03-31
Primary Completion
2021-02-06
Completion
2021-02-06

Countries

  • Argentina
  • Brazil
  • Colombia

Study Locations

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Entities

Diseases
Companies

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT03872531 on ClinicalTrials.gov