A Study to Prospectively Assess Disease Progression in Male Children With X-ALD
NCT03278899 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 100
Last updated 2018-08-08
Summary
This is a non-interventional, multi-center study that follows general principles of periodic assessment of X-ALD patients in routine practice. No study drug treatment will be given and no changes to patient treatment are necessary.
Conditions
- X-Linked Adrenoleukodystrophy
Sponsors & Collaborators
-
NeuroVia, Inc.
lead INDUSTRY
Principal Investigators
-
John Henderson, MD · NeuroVia, Inc.
Eligibility
- Min Age
- 2 Years
- Max Age
- 13 Years
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2018-02-16
- Primary Completion
- 2021-06-01
- Completion
- 2021-06-01
Countries
- United States
Study Locations
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