A Study to Learn About Metachromatic Leukodystrophy (MLD) in Children in Spain
NCT05755568 · Status: WITHDRAWN · Type: OBSERVATIONAL
Last updated 2024-01-12
Summary
The main aim of this study is to learn about metachromatic leukodystrophy (MLD) in children and teenagers in Spain. This includes checking the number of new MLD cases and the frequency of children with MLD in 2022 in Spain.
There is no treatment involved in this study. Participants' data will be taken from their medical records (charts), which were already collected as a part of their routine care between 01 January 2000 and 31 December 2022.
Conditions
- Metachromatic Leukodystrophy (MLD)
Interventions
- OTHER
-
No Intervention
As this is an observational study, no intervention will be administered.
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Study Director · Takeda
Eligibility
- Min Age
- 0 Years
- Max Age
- 15 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2023-11-30
- Primary Completion
- 2024-07-01
- Completion
- 2024-07-01
Countries
- Spain
Study Locations
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