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Natural History Study of Children With Metachromatic Leukodystrophy

NCT01963650 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 1

Last updated 2021-03-17

No results posted yet for this study

Summary

The purpose of this study is evaluate the natural course of disease progression related to gross motor function in children with metachromatic leukodystrophy (MLD).

Conditions

  • Lipid Metabolism Disorders
  • Metachromatic Leukodystrophy (MLD)
  • Nervous System Diseases
  • Brain Diseases
  • Central Nervous System Diseases
  • Demyelinating Diseases
  • Metabolism, Inborn Errors
  • Genetic Diseases, Inborn
  • Sphingolipidoses
  • Hereditary Central Nervous System Demyelinating Diseases
  • Metabolic Inborn Brain Diseases
  • Lysosomal Storage Diseases
  • Metabolic Diseases
  • Sulfatidosis

Sponsors & Collaborators

  • Shire

    lead INDUSTRY

Principal Investigators

  • Study Director · Takeda

Eligibility

Max Age
12 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2015-11-02
Primary Completion
2016-04-08
Completion
2016-04-08

Countries

  • United States
  • Argentina
  • Belgium
  • Brazil
  • Canada
  • Denmark
  • France
  • Germany
  • Japan
  • Turkey (Türkiye)

Study Locations

More Related Trials

Entities

Diseases

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT01963650 on ClinicalTrials.gov