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The Natural History of Infantile Globoid Cell Leukodystrophy

NCT00983879 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 6

Last updated 2018-03-08

No results posted yet for this study

Summary

The purpose of this natural history study is to understand more about the progression of infantile Krabbe disease, a very rare genetic disease. There is very little published longitudinal data with only anecdotal cases. This natural history study will be important in understanding the effect of future therapies that are presently in the preclinical phase.

Conditions

  • Infantile Globoid Cell Leukodystrophy

Sponsors & Collaborators

  • Zymenex A/S

    lead INDUSTRY

Principal Investigators

  • Maria L Escolar, MD · NFRD Office, Pittsburgh, Pennsylvania, US

Eligibility

Max Age
2 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2009-09-30
Primary Completion
2014-07-31
Completion
2014-07-31

Countries

  • United States

Study Locations

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Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT00983879 on ClinicalTrials.gov