The Natural History Study of Patients With Sanfilippo Disease(s) (MPS3)
NCT05705674 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 6
Last updated 2024-03-12
Summary
The natural history study of patients with Sanfilippo disease(s) (MPS3)
Conditions
- Sanfilippo Syndrome
- MPS3
Sponsors & Collaborators
-
Team Sanfilippo
collaborator UNKNOWN -
Lysosomal and Rare Disorders Research and Treatment Center, Inc.
lead OTHER
Eligibility
- Min Age
- 5 Years
- Max Age
- 99 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2023-05-01
- Primary Completion
- 2024-12-31
- Completion
- 2024-12-31
Countries
- United States
Study Locations
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