Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia
NCT06560346 · Status: WITHDRAWN · Type: OBSERVATIONAL
Last updated 2025-06-08
Summary
Multicenter, prospective, observational natural history and outcome measure study of children and young adults with Friedreich ataxia.
Conditions
- Friedreich Ataxia
- Rare Diseases
Interventions
- OTHER
-
Geneticlly confirmed disease causing FXN mutatuion
No intervention in this observational Natural History Study
- OTHER
-
Healthy Control
No intervention in this observational Natural History Study
Sponsors & Collaborators
-
Friedreich's Ataxia Research Alliance
lead OTHER
Principal Investigators
-
Jennifer Farmer · Friedreich's Ataxia Research Alliance
Eligibility
- Min Age
- 4 Years
- Max Age
- 21 Years
- Sex
- ALL
- Healthy Volunteers
- Yes
Timeline & Regulatory
- Start
- 2025-05-01
- Primary Completion
- 2028-12-01
- Completion
- 2028-12-01
Countries
- United States
- Australia
- Canada
- Germany
- Italy
Study Locations
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