Bone Marrow for Hemoglobinopathy Research
NCT00669305 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 26
Last updated 2020-02-25
Summary
Human participants affected with sickle cell disease or thalassemia will donate bone marrow for use in experimental laboratory models to study potential new treatments. This is an observational study using bone marrow from human participants. The investigators will use sickle cell and thalassemia mouse models to observe and evaluate the possibility of correcting these disorders through genetic alterations or drug treatment.
Conditions
Sponsors & Collaborators
-
National Heart, Lung, and Blood Institute (NHLBI)
collaborator NIH -
Assisi Foundation
collaborator OTHER -
University of Tennessee
collaborator OTHER -
St. Jude Children's Research Hospital
lead OTHER
Principal Investigators
-
Mitchell J. Weiss, MD, PhD · St. Jude Children's Research Hospital
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2008-05-15
- Primary Completion
- 2019-08-29
- Completion
- 2019-08-29
Countries
- United States
Study Locations
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