Thalassemia refers to inherited hemoglobin disorders with reduced or absent globin-chain production, causing microcytic anemia and variable severity from asymptomatic carrier states to transfusion-dependent disease.
Healthcare sector surged 10% since Q4 2025, outpacing all S&P 500 sectors as investors rotate from tech to pharmaceutical value plays. Major drugmakers demonstrate resilience following Medicare price negotiations implementation.
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March of Dimes awarded the 2026 Richard B Johnston Jr, MD Prize to hematologist Leonard Zon for pioneering zebrafish research that illuminated blood development in embryos and led to breakthrough treatments for genetic blood disorders in children.
| NCT ID | Title | Status | Phase |
|---|---|---|---|
| NCT07579949 |
A Study of SNH-119014 in Adult Participants With Non-transfusion-dependent Thalassemia (NTDT) |
NOT_YET_RECRUITING | PHASE2 |
| NCT07352878 |
Evaluation of the Quality of Life in Patients With Chronic Iron Overload Due to Hemoglobinopathies in Greece. |
NOT_YET_RECRUITING | |
| NCT07210450 |
Effect of L-Glutamine on Pulmonary Artery Pressure in Patients With Non-Transfusion-Dependent Thalassemia |
COMPLETED | PHASE2/PHASE3 |
| NCT07099196 |
Impact of Virtual Reality on Pain and Anxiety During Intravenous Cannulation Procedures Among Thalassemia Patients in UAE. |
COMPLETED | NA |
| NCT07064941 |
Effect of Exercise on Body Composition and Bone Health in Patients With Thalassemia |
RECRUITING | NA |
| NCT07023029 |
A Study on the Effect of Etavopivat on Heart Rhythm in Healthy Participants |
COMPLETED | PHASE1 |
| NCT06889727 |
Pregnancy and Childbirth in Women with Thalassemia Yesterday and Today |
COMPLETED | |
| NCT06888232 |
Safety and Efficacy of Immunomodulator Drug Thalidomide in Multi-transfused Thalassemia Patients |
COMPLETED | NA |
| NCT06800495 |
Development of THALEA Kit and Its Impact on Knowledge, Attitude, and Intention for Premarital Thalassemia Screening |
ACTIVE_NOT_RECRUITING | NA |
| NCT06609226 |
A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia |
RECRUITING | PHASE3 |
