Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
- Status
- RECRUITING
- Phase
- PHASE3
Clinical Trials Related to Thalassemia
Related studies linked through entity extraction aliases.
Hemoglobinopathy Nursing Program and Pediatric Nursing Students
- Status
- COMPLETED
- Phase
- NA
Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE3
Long-term Clinical Study of CN128 in Thalassemia With Sever Liver Iron Overloaded Patients
- Status
- COMPLETED
- Phase
- PHASE2
Inhibitory Effect of a Polyphenol Supplement on Dietary Iron Absorption in Adults with Thalassemia
- Status
- COMPLETED
- Phase
- NA
Red Blood Cell - IMProving trAnsfusions for Chronically Transfused Recipients
- Status
- COMPLETED
- Phase
- N/A
A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease
- Status
- COMPLETED
- Phase
- PHASE2
Thalassemia Knowledge in Young People of Indonesia
- Status
- UNKNOWN
- Phase
- N/A
Long-term Clinical Study of CN128 in Thalassemia Patients
- Status
- COMPLETED
- Phase
- PHASE2
The Role of OCTA in Patients Affected by Beta Thalassemia
- Status
- COMPLETED
- Phase
- N/A
ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
- Status
- RECRUITING
- Phase
- N/A
Effect of Folic Acid Supplementation in Pregnant Women Having Thalassaemia Trait
- Status
- NOT_YET_RECRUITING
- Phase
- NA
A Long-term Follow-up Study in Participants Who Received CTX001
- Status
- ENROLLING_BY_INVITATION
- Phase
- PHASE3
Short-term Clinical Study of CN128 in Thalassemia Patients
- Status
- COMPLETED
- Phase
- PHASE1
Immunomodulatory Vitamin D in Thalassemia
- Status
- COMPLETED
- Phase
- NA
Hydroxyurea Therapy: Optimizing Access in Pediatric Populations Everywhere
- Status
- TERMINATED
- Phase
- PHASE2
Long Term Follow-up Study for Patients Enrolled on the BP-004 Clinical Study
- Status
- TERMINATED
- Phase
- PHASE1/PHASE2
iHSCs With the Gene Correction of HBB Intervent Subjests With β-thalassemia Mutations
- Status
- UNKNOWN
- Phase
- EARLY_PHASE1
Cerebrovascular Reserve and White Matter Disease in Patients with Chronic Anemia
- Status
- COMPLETED
- Phase
- N/A
A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE2