315 participants
Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care
- Study Type:
- OBSERVATIONAL
- Last Updated:
- 2024-09-19
- Start Date:
- 2013-09-30
- Completion:
- 2019-09-30
Conditions
- Hereditary Tyrosinemia, Type I
Interventions
- DRUG
No Results Yet