An Observational Study in Children and Adults With Stargardt Disease
NCT06591806 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 80
Last updated 2025-08-28
Summary
This multicenter, prospective, longitudinal, observational study in approximately 80 subjects with Stargardt disease secondary to biallelic mutations in the ABCA4 gene (STGD1) aims to evaluate prognostic factors of disease progression, and to further characterize the patient population for future clinical studies.
Conditions
Sponsors & Collaborators
-
AAVantgarde Bio Srl
lead INDUSTRY
Eligibility
- Min Age
- 8 Years
- Max Age
- 50 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2024-05-01
- Primary Completion
- 2027-06-30
- Completion
- 2027-06-30
Countries
- United States
- Norway
Study Locations
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