Natural History and Functional Status Study of Patients With Lafora Disease
NCT03876522 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 33
Last updated 2022-09-28
Summary
A natural history and functional status study to characterize the clinical disease course in Lafora disease patients using standardized, quantitative evaluations and to identify useful biomarkers and clinical outcome measures for use in future Lafora treatment studies.
Conditions
- Lafora Disease
Sponsors & Collaborators
-
Ionis Pharmaceuticals, Inc.
lead INDUSTRY
Eligibility
- Min Age
- 5 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2019-01-09
- Primary Completion
- 2022-04-01
- Completion
- 2022-04-01
Countries
- United States
- Italy
- Spain
Study Locations
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