Treatment With UX007 for a Single Patient With GLUT1 Deficiency Syndrome
NCT02968953 · Status: NO_LONGER_AVAILABLE · Type: EXPANDED_ACCESS
Last updated 2019-02-08
Summary
This treatment plan is intended for the use of UX007 (triheptanoin) in the treatment of a single patient with Glucose Transporter 1 (GLUT1) Deficiency Syndrome.
Conditions
- Glucose Transporter 1 Deficiency Syndrome
Interventions
- DRUG
-
Triheptanoin
A single patient with Glucose Transporter 1 (GLUT1) Deficiency Syndrome will receive tripheptanoin (UX007).
Sponsors & Collaborators
- collaborator INDUSTRY
-
Jerry Vockley, MD, PhD
lead OTHER
Principal Investigators
-
Gerard Vockley, MD, PhD · University of Pittsburgh
Eligibility
- Min Age
- 3 Years
- Sex
- FEMALE
- Healthy Volunteers
- No
Timeline & Regulatory
Countries
- United States
Study Locations
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